Hemophilia and Rare Bleeding Disorders » Hemophilia - Basic

Abstract Number: PB0491

A Review Following Implemented Training for Health Care Practitioners in Primary Care Settings of Immunisation Practice in Children with Bleeding Disorders

M. Eales¹, A. Wilkinson¹, S. Pool², G.W Hall¹, N. Bhatnagar¹

Abstract Number: PB0493

Acute Myelogenous Leukemia in a Patient with Mild Haemophilia A. A Case Report at Hospital Infantil de México Federico Gómez

L.M. Muñoz Juárez Díaz¹, A.M. Moreno Gonzalez¹, L. Velázquez Marmolejo¹

Abstract Number: OC 24.4

Altered vWF-FVIII Binding Modulates the Factor VIII Immune Response

S.M. Zintner¹, R.J. Davidson¹, A.R. Wilhelm¹, R.M. Camire^1,2,3, L.A. George^1,3,2

Abstract Number: PB0481

Analysis of the Percentage of Persons with Severe Hemophilia A as an Indicator of Care

E. Tootoonchian¹, J. Stonebraker², M. El Ekiaby³, E. Gouider⁴, A. Iorio⁵, M. Makris⁶, J. O'Hara⁷, M. Recht⁸, G. Pierce¹, D. Coffin¹

Abstract Number: PB0476

Association between Factor VIII Deficiency and Low Bone Mineral Density in Children with Hemophilia

O.U. Galindo-Aguilar¹, P.A. García-Hernández², J.Á. Garza³, D. Garay-Mendoza⁴, M. Ortiz-Castillo⁵, A. González-Martínez⁵, A.J. Bautista-Gómez⁵, G. González-Martínez⁵, J.F. Molina-de la Garza⁵, L. Villarreal Martínez⁵

Abstract Number: OC 38.3

BAFF Inhibition Prevents FVIII Inhibitor Formation in a Marginal Zone B Cell-independent Manner

B. Doshi^1,2, M. Shaheen², V. Arruda^1,2

Abstract Number: OC 49.1

Bone Disease in Hemophilia: The Role of Different Bone Cells

S. Lancellotti¹, G. Battafarano², M. Sacco³, M. Tardugno³, L. Di Gennaro¹, R. De Cristofaro^1,3, A. Del Fattore²

Abstract Number: PB0486

Characteristics of Anti-drug Antibody against Emicizumab Analyzed Using Hemophilia A Patient-derived Plasma Samples

R. Kawasaki¹, M. Kaneda², M. Noguchi¹, N. Matsumoto¹, H. Abe¹, Y. Tashiro¹, Y. Inokuchi¹, H. Yasuno¹, T. Soeda¹, Y. Yoshimura¹, T. Oka²

Abstract Number: PB0473

Clinical Characteristics and Incidence of Inhibitors in Previously Untreated Children with Haemophilia: An Update of the Hemfil Cohort Study

L.L. Jardim^1,2, M. Antônio Portugal Santana3³, D. Gonçalves Chaves⁴, L. Werneck Zucheratto¹, M. Hermida Cerqueira⁵, C. Santos Lorenzato⁶, V. Franco⁷, J. van der Bom², S. Meireles Rezende¹

Abstract Number: PB0492

Clinical Profile and Bleeding Outcome of Pediatric Hemophilia A: The Royal Hospital’s Experience, Oman

A. Al Rawahi¹, F. Al Riyami², I. Al Ghaithi³, H. Al Shukaili⁴, M. Al Abri⁴, A. Al Rawahi⁵

Abstract Number: OC 56.2

Comparative Analysis of Residual Factor VIII Expression from Recurrent F8 Nonsense Mutations Indicates that Localization in the B-domain Favours Readthrough-mediated Protein Output

M.F. Testa¹, S. Lombardi¹, M. Ferrarese¹, P. Radossi², D. Belvini², G. Castaman³, F. Bernardi¹, M. Pinotti¹, A. Branchini¹

Abstract Number: PB0471

Comparative Recovery of FVIII Antigen with Various FVIII Therapeutic Concentrates Using an Improved 2^nd Generation ELISA Kit

R. Ni¹, P. Erb¹, J. Della Maestra¹, H. Atkinson², D. Foulon¹, K.M Black³, H. Hoogendoorn¹, D. Matino^2,4

Abstract Number: OC 56.1

Deep Molecular Mechanisms of F8 exon 19 Variants and Translational Approaches in Hemophilia A

S. Lombardi¹, L. Peretto¹, S. Merlin², A. Follenzi², J.H. McVey³, I. Maestri¹, F. Bernardi¹, M. Pinotti¹, D. Balestra¹

Abstract Number: PB0477

Differences in Thrombin Generating Capacity in Severe Haemophilia A

C. Hamid^1,2, J. Dunster³, E. Aradom¹, J. McVey⁴, P. Chowdary^1,2

Abstract Number: PB0469

Dose Selection for Subcutaneous Marzeptacog Alfa (Activated) in Subjects with Factor Vll Deficiency Using Population Pharmacometric Clinical Trial Simulations

A. Faraj¹, S. Desai², L. Neuman², G.E Blouse², T. Knudsen², U.S. Simonsson¹

Abstract Number: PB0458

Dose Selection of Marzeptacog Alfa (Activated) in Children with Hemophilia: A Population Pharmacokinetic Exposure Matching Strategy

A. Faraj¹, R. van Wijk¹, L. Neuman², S. Desai², G.E Blouse², T. Knudsen², U.S. Simonsson¹

Abstract Number: PB0467

Effects of von Willebrand Factor on Plasma Haemostasis

C. Kluft¹, K. Van Leuven¹, C. Krijnen¹, P. De Kruijf¹

Abstract Number: PB0482

Evaluation of Primary Haemostasis in Children and Young Adults with Haemophilia

M. Kürschner¹, J. Lohse¹, F. Boiti¹, O. Tiebel², R. Knöfler¹

Abstract Number: OC 24.1

Evaluation of the Tissue Factor-Independent Mechanism of Action for Eptacog Beta

J.-L. Plantier¹, S. Evans², P. Martres¹

Abstract Number: PB0468

Examination and Validation of a Patient-centric Joint Metric: “PROBLEM JOINT”; Empirical Evidence from the CHESS Paediatrics Dataset

T. Burke¹, I. Rodriguez Santana¹, P. Chowdary², R. Curtis³, K. Khair⁴, M. Laffan⁵, P. McLaughlin², D. Noone¹, B. O'Mahony⁶, J. Pasi⁷, M.W Skinner⁸, J. O'Hara¹